Dawnzera is the first and so far only RNA-targeting therapy approved as a prophylactic treatment for hereditary angioedema ...

Yale researchers have developed a new and safe family of RNA-editing tools that utilize an RNA-targeting activity that they ...

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

The US Food and Drug Administration (FDA) has approved Dawnzera (donidalorsen) for prophylaxis to prevent attacks of ...

Studying the process of brain formation illuminates just how much of development is a series of tiny miracles. Only a few ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has approved ...

"I am saddened and outraged that more citizens are not tuning into this war against scientific health research in the United ...

In the past decade, there has been significant interest in studying the expression of our genetic code down to the level of ...

Skyhawk's RNA tech could be Merck's next blockbuster play as drug setbacks and looming patent cliffs force a reinvention.

Single-cell proteomics with RNA sequencing uncover hidden gene expression dynamics in stem cell differentiation.