"In many countries, health insurance changes when DMD men are no longer seen in a specialized pediatric center. This impacts massively on the quality of care they receive. For this reason, many DMD ...
ST. LOUIS — On a beautiful day in Forest Park, dozens of people brought hope to kids and adults with Muscular Dystrophy by just taking a long walk. The Muscular Dystrophy Association used the walk to ...
The only gene replacement therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA).
Editor’s note: This is an automatically generated transcript. Please notify editor@healio.com if there are concerns regarding accuracy of the transcription. Patient advocacy organizations often bring ...
New York, Oct. 18, 2023 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) celebrates the US Food and Drug Administration (FDA) approval of ZILBRYSQ ® zilucoplan for the treatment of ...
Adults with Duchenne muscular dystrophy demonstrated functional improvements exceeding natural history, following 28-day treatment with SAT-3247 Grip strength increased 118.6% and predicted forced ...
The compound called Cugamycin works by recognizing toxic RNA repeats and destroying the garbled gene transcript. People diagnosed with myotonic dystrophy type 1 have difficulty unclenching muscles due ...
People diagnosed with myotonic dystrophy type 1 have difficulty unclenching muscles due to a genetic defect that generates toxic material within their cells. There is currently no treatment. In a new ...
Medical Care, Vol. 52, No. 10, SUPPLEMENT 3: Healthcare at the Intersection of Disability, Race, and Ethnicity (October 2014), pp. S32-S39 (8 pages) Background: For people with muscular dystrophy (MD) ...
TORONTO, October 21, 2025--(BUSINESS WIRE)--Satellos Bioscience Inc. (TSX: MSCL, OTCQB: MSCLF) ("Satellos" or the "Company"), a clinical-stage biotechnology company developing life-improving medicines ...
JUPITER, Fla. - April 1, 2019 -- People diagnosed with myotonic dystrophy type 1 have difficulty unclenching muscles due to a genetic defect that generates toxic material within their cells. There is ...
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